Abi Nader, Khalil; David, Anna L.; McIntosh, Jenny; Peebles, Donald; Cook, Terry; Waddington, Simon; Weisz, Boaz
(2016-06-07)
Somatic in utero gene therapy aims to treat congenital diseases where pathology develops in perinatal life, thereby preventing permanent damage. The aim of this study was to determine whether delivery of self-complementary ...